RARECast

548 Episodo

1. Accelerating the Development of Genetic Medicines with AI

   Publicado: 7/12/2023
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Publicado: 30/11/2023
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Publicado: 22/11/2023
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Publicado: 16/11/2023
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Publicado: 9/11/2023
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Publicado: 2/11/2023
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Publicado: 26/10/2023
8. Turning Grief into Action

   Publicado: 19/10/2023
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Publicado: 12/10/2023
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Publicado: 5/10/2023
11. A Genetic Counselor’s Journey into Patient Advocacy

    Publicado: 28/9/2023
12. A Company in the Fold of Rare Disease

    Publicado: 21/9/2023
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Publicado: 14/9/2023
14. Keeping the Sentinels of the Brain Vigilant

    Publicado: 7/9/2023
15. Considering the Unfinished Work in Cystic Fibrosis

    Publicado: 31/8/2023
16. How to Advocate for Yourself as You Battle Cancer

    Publicado: 24/8/2023
17. Targeting Neuroinflammation to Treat ALS

    Publicado: 17/8/2023
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Publicado: 10/8/2023
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Publicado: 3/8/2023
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Publicado: 27/7/2023